Preclinical testing of 3 cysteine-related drugs for reducing dystropathology in the mdx mouse model of Duchenne Muscular Dystrophy [ 2014 - 2017 ]

Research Grant

Researchers: Dr Peter Arthur (Principal investigator) ,  Prof Miranda Grounds

Brief description Duchenne muscular dystrophy (DMD) is devastating disease that affects young boys. We propose testing 3 cysteine related drugs which show promise in ameliorating the severity of the disease. The drugs are of particular interest because they are relatively inexpensive, can be taken orally, have few side effects and are already approved for human use. These drugs will tested in an animal model of DMD to test their efficacy.

Funding Amount $AUD 378,564.43

Funding Scheme Project Grants

Notes Standard Project Grant